Research

Hormonal

Myostatin acts as a negative regulator of skeletal muscle mass by inhibiting protein synthesis and promoting degradation; blocking myostatin signaling increases muscle mass in animal models but has failed to show clinical efficacy in elevating muscle strength in human muscular dystrophy trials.

While myostatin is a key regulator of muscle size, simply targeting it (e.g., via drugs or genetic mutation) increases mass but has not reliably improved strength in human clinical trials. Current research suggests targeting myostatin alone is insufficient for treating muscle wasting in humans, and other factors like activin A may play larger roles in primates.

ModerateQualifiesMEDIUM confidence
Functionally, myostatin is a negative regulator of muscle growth thereby leading to inhibition of myogenesis... Animals blocking myostatin activity with substance show significantly increased muscle mass... In humans, individuals with mutations in both copies of the myostatin gene showed significantly increased muscle mass and muscle strength... However, so far none of these treatments have proven to be clinically sufficient... a myostatin antibody, MYO-029/stamulumab, was tested in broad muscle dystrophic models... but failed to show clinical efficacy in elevating muscle strength.
Jong Han Lee et al. · Frontiers in Physiology · 2019

Why this rating

Strong mechanistic evidence in animals and genetic cases, but weak/failed clinical trial evidence in humans for strength outcomes.

Source

Role of Myokines in Regulating Skeletal Muscle Mass and Function

Jong Han Lee et al. · Frontiers in Physiology · 2019

DOI 10.3389/fphys.2019.00042

narrative_reviewCited 425×
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DOI resolved against Crossref · corpus check 2026-06-10

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